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genetic diseases
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A Collaboration and License Agreement Focused on The Development of Therapeutics
Jan 10, 2014Biogen Idec (NASDAQ: BIIB) and Sangamo BioSciences, Inc. (NASDAQ: SGMO) announced today an exclusive worldwide collaboration and license agreement focused on the development of therapeutics for hemoglobinopathies, inherited conditions that ...
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A Powerful Technique to Visualize The Shape and Motion of RNA
Jan 10, 2014Qi Zhang sees himself as a warrior. In his lab at the University of North Carolina at Chapel Hill, he wages war on genetic diseases such as cancer and heart disease on a battlefield measured with single atoms. In a paper published by the ...
Tags: genetic diseases, RNA, nuclear magnetic resonance spectroscopy
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A Ludwig Cancer Research Study Has Uncovered a Phenomenon
Jan 10, 2014A Ludwig Cancer Research study has uncovered a phenomenon that alters prevailing views of how the genome is expressed to make and sustain the life of mammals. Published in the journal Science, the paper helps explain why genetically ...
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OvaScience and Intrexon Corporation Have Announced an Agreement
Dec 23, 2013OvaScience, a life sciences company, and Intrexon Corporation have announced an agreement to access Intrexon’s portfolio of technologies to accelerate the development of OvaScience’s OvaTure technology platform Separately, ...
Tags: OvaScience, Infertility Treatments
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arGEN-X Has Achieved a Key Success Milestone
Sep 19, 2013arGEN-X, a clinical stage human monoclonal antibody therapeutics company, cin its SIMPLE Antibody research program collaboration with Shire Pharmaceuticals' Human Genetic Therapies division. The milestone, which was the first ...
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Inherited Diseases Are The Passing of Bad Characteristics From Generation to Generation
Sep 10, 2013A disease, by definition, is a disorder of structure or function in an organism that produces specific symptoms or signs to indicate its presence. Inheritance, in terms of biology, is the passing of characteristics, good or bad, from ...
Tags: Inherited Blood Diseases, Health, Medicine
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Syngen Received 510(K) Approval From The US FDA to Market Its Syngenx-1000 System
Jul 17, 2013SynGen has received 510(k) approval from the US Food and Drug Administration (FDA) to market its SynGenX-1000 System, CryoPRO-2 Cryopreservation/Storage Bag Set, SynGen DataTrak software products to process cord blood. Previously, the ...
Tags: Cord Blood Processing, Syngen
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Nimbus Discovery Has Entered Into a Co-Development Agreement with Shire
May 13, 2013Nimbus Discovery, a US-based biotechnology company, has entered into a co-development agreement with Shire aiming at small molecule treatments for lysosomal storage disorders (LSDs), which are considered as the rare genetic diseases. The ...
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GSC's Disease-Specific Human Stem Cells Have Been Placed on The USA NIH
Jan 22, 2013Genea Stem Cells Pty Ltd (GSC), a supplier and developer of disease-specific human stem cells, has announced that 25 of its disease specific embryonic pluripotent stem cell lines have been placed on the USA National Institutes of Health ...
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Repligen Has Announced a New Licensing Agreement with Pfizer
Jan 4, 2013Repligen has announced a new licensing agreement with Pfizer in an effort to advance Repligen's spinal muscular atrophy (SMA) program. The work focuses on RG3039, which is a small molecule drug candidate in clinical development for the ...
Tags: Repligen, Pfizer, spinal muscular atrophy, Medicine
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A Sequencing Protocol Using a Rapid-Throughput Platform Could Help Diagnose Ill Infants
Dec 11, 2012Illumina system used in faster genome sequencing 08 Oct 2012 A sequencing protocol using a rapid-throughput platform could help diagnose critically ill infants. Faster sequencing Investigators at Kansas City's Children's Mercy ...
Tags: Illumina system, Science Translational Medicine, test, health
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REGENX Biosciences Has Received FDA Orphan Drug Designation
Apr 11, 2012REGENX BioSciences has received FDA orphan drug designation for treatment of familial hypercholesterolemia (HoFH) using NAV rAAV8 vectors. The REGENX program consists of a NAV rAAV8 vector expressing a normal copy of the human ...
Tags: orphan drug designation, familial hypercholesterolemia, clinical study
